twitter logo linkedin logo facebook logo youtube logo instagram logo search icon star icon United Kingdom Flag Netherlands Flag Germany Flag France Flag Italy Flag Switzerland Flag Canada Flag Belgium Flag Denmark Flag Finland Flag Greece Flag Ireland Flag Sweden Flag Portugal Flag Spain Flag Skip to content
  • Language
    • English
    • Deutsch
    • Français
    • Español
    • Italiano
  • Swiss offering
  • Global offering
  • Services
    • Services
    • End-to-end dispense and delivery
      • Supply chain management
      • Pharmaceutical storage and distribution
      • Dispense and delivery
    • Treatment delivery and ongoing engagement
      • Digital solutions
      • Patient support programmes
      • Nursing and clinical services
      • Clinical homecare
    • Clinical study support and real-world evidence
      • Real-world data
      • Early access programmes
      • Pharmacovigilance services
      • Clinical trials
    • Health system efficiencies
      • Cancer care at home
      • Blood monitoring services
      • E-prescription services
      • Non-medical prescribing services
      • Clinical screening services
      • Switching services
    • Market access support
      • Early access programme services
      • Regulatory approval consulting
    • Cancer services
      • Aseptic compounding
      • Cancer care at home
  • Digital innovation
  • Therapeutic areas
    • Therapeutic areasOur key therapeutic areas focus on, cancer, chronic conditions, rare and speciality diseases.
    • Cancer services
    • Chronic conditions
    • Rare & speciality
  • Knowledge base
    • Knowledge baseStay up-to-date with the latest industry news, trends, insights and research. This section provides valuable information and resources.
    • Thought leadership
    • Case studies
    • Blogs
    • Events
    • News
  • About us
    • About usA leading life sciences organisation proudly sitting at the intersection of patients and their medicine.
    • Our locations
    • Careers
    • Executive team
    • Meet our experts
    • Partnerships
      • Partnerships
      • NHS
      • Healthcare professionals
      • Biopharma
    • Our Commitments
      • Patient care and safety
      • Health regulations and standards
      • Environmental, social and governance strategy
  • Contact us

Heading to the Biotech Showcase 2026? Connect with our team to explore how we can help you unlock Europe.

  • English
    • English
    • Deutsch
    • Français
    • Español
    • Italiano
  • Swiss offering
  • Global offering
  • Language
    • English
    • Deutsch
    • Français
    • Español
    • Italiano
  • Swiss offering
  • Global offering
  • Services
    • Services
    • End-to-end dispense and delivery
      • Supply chain management
      • Pharmaceutical storage and distribution
      • Dispense and delivery
    • Treatment delivery and ongoing engagement
      • Digital solutions
      • Patient support programmes
      • Nursing and clinical services
      • Clinical homecare
    • Clinical study support and real-world evidence
      • Real-world data
      • Early access programmes
      • Pharmacovigilance services
      • Clinical trials
    • Health system efficiencies
      • Cancer care at home
      • Blood monitoring services
      • E-prescription services
      • Non-medical prescribing services
      • Clinical screening services
      • Switching services
    • Market access support
      • Early access programme services
      • Regulatory approval consulting
    • Cancer services
      • Aseptic compounding
      • Cancer care at home
  • Digital innovation
  • Therapeutic areas
    • Therapeutic areasOur key therapeutic areas focus on, cancer, chronic conditions, rare and speciality diseases.
    • Cancer services
    • Chronic conditions
    • Rare & speciality
  • Knowledge base
    • Knowledge baseStay up-to-date with the latest industry news, trends, insights and research. This section provides valuable information and resources.
    • Thought leadership
    • Case studies
    • Blogs
    • Events
    • News
  • About us
    • About usA leading life sciences organisation proudly sitting at the intersection of patients and their medicine.
    • Our locations
    • Careers
    • Executive team
    • Meet our experts
    • Partnerships
      • Partnerships
      • NHS
      • Healthcare professionals
      • Biopharma
    • Our Commitments
      • Patient care and safety
      • Health regulations and standards
      • Environmental, social and governance strategy
  • Contact us
Patient hub Contact us
  • Home
  • Knowledge base
  • Rare diseases

Rare diseases

Expansion into new international biotech markets can be challenging. Unfamiliar regulations and licensing, coupled with language and cultural differences, can all be barriers to growth. If you’re considering venturing into Europe and beyond, our easy-to-follow guides, shaped by 30 years of expertise in the rare disease market, will assist you in navigating challenges and gaining a profound understanding of the complexities involved in launching orphan drugs into new markets. To learn more about how Sciensus can facilitate and support your Europan expansion, visit: Rare Diseases and Orphan Drugs

or

View all

News

Rare diseases

Sciensus names Julie Gosper as Managing Director, Rare & Specialty, to accelerate biopharma access to European markets

Thought Leadership

Rare diseases

From innovation to access: securing the last mile in rare disease

Blogs

Rare diseases

Patient engagement and in‑market support: best practices post‑approval 

Blogs

Rare diseases

Early/expanded access programmes: Making rare treatments accessible ethically and efficiently in Europe

Thought Leadership

Rare diseases

Rare disease launch insights report

Logo for the World Orphan Drug Congress Europe 2025

Events

Rare diseases

We’re speaking at the WODC EU 2025

Empowering the patient voice

Thought Leadership

Rare diseases

Empowering the patient voice

Events

Rare diseases

We’re speaking at the Rare Trials Summit 2025

Case Studies

Rare diseases

How Sciensus supported the launch and distribution of a breakthrough therapy in Europe and beyond

  • 1
  • 2
  • 3
  • …
  • 6
  • Next results

Get in touch with Sciensus

If you have a question, or would like to know more about any aspect of what we do, please visit the contact page to get in touch.

Contact us
About us
  • About us
  • Environmental, social & governance
  • Our locations
  • Careers
Partners
  • Pharmaceutical and biotech companies
  • NHS
  • Healthcare professionals
Help & contact
  • Patient enquiry
  • Patient hub
  • Contact us
  • Partnership queries
Legal & regulatory
  • Privacy notices
  • Cookie notice
  • Terms and conditions
  • Accessibility statement
  • Gender pay gap report
  • Modern slavery statement
  • Tax strategy
  • Annual duty of candour report
  • Anti-fraud statement
Registered Pharmacies

Fifth Avenue, Centrum 100, Burton-on-Trent, Staffordshire, DE14 2WS, UK

General Pharmaceutical Council Registration 1084907

Plot 7, Junction Close, Green Lane Industrial Park, Featherstone, Pontefract, West Yorkshire, WF7 6ER, UK

General Pharmaceutical
Council Registration 1092334

Twitter logo Linkedin logo Facebook logo Youtube logo
  • Privacy notices
  • Terms and conditions

©2026 - Sciensus | All rights reserved