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Heading to World Orphan Drug Congress in Boston? Learn how we can help accelerate access to patients in Europe. Talk to our team

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    • Switzerland
Contact us
  • Region
    • Switzerland
  • Services
  • Therapeutic areas
    • Therapeutic areasOur key therapeutic areas focus on, cancer, long-term conditions and rare and orphan diseases.
    • Cancer
    • Long-term conditions
    • Rare and orphan diseases
      • Early access program services
      • Real-world data
      • Supply chain management
      • Regulatory services
      • Patient support programs
      • Market access
  • Knowledge hub
    • Knowledge hubStay up-to-date with the latest industry news, trends, insights and research. This section provides valuable information and resources.
    • Thought leaderships
    • Case studies
    • Blogs
    • Events
    • News
    • Patient stories
  • Patient hub
    • Patient hubA one-stop destination for patients to access all the essential information about our services.
    • Patient resources
    • Patient help centre
    • Life stories
    • Sciensus Intouch app
    • For new patients
      • New Patients: Where to start and what to expect
      • For cancer patients
  • Digital+
    • Digital+Digital+ is a suite of digital products and services designed to enhance patient care and improve their health outcomes.
    • Digital solutions
      • Sciensus Intouch app
      • Sciensus Cancer Companion app
      • SciensusPRO
      • Healthcare products (via Sciensus Axcess)
      • Online communities
      • Sciensus Connect
    • Patient support programs
    • Real-world data
  • About us
    • About usA leading life sciences organisation proudly sitting at the intersection of patients and their medicine.
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Rare diseases

Expansion into new international biotech markets can be challenging. Unfamiliar regulations and licensing, coupled with language and cultural differences, can all be barriers to growth. If you’re considering venturing into Europe and beyond, our easy-to-follow guides, shaped by 30 years of expertise in the rare disease market, will assist you in navigating challenges and gaining a profound understanding of the complexities involved in launching orphan drugs into new markets. To learn more about how Sciensus can facilitate and support your Europan expansion, visit: Rare Diseases and Orphan Drugs

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Blogs

How to set up an EAP without a European presence 

Expanded Access Programs

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EMA orphan drug designation

real-world data

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Four considerations before collecting real-world data in your EAP

rare and orphan diseases

Blogs

The increasing importance of real-world data for the EMA

Real-world data

Blogs

Real-world data and shaping the future of healthcare 

early access program benefits

Blogs

Six steps for a successful Early Access Program in Europe 

patient support program in europe

Thought Leadership

Get the free whitepaper: Transitioning from open-label extensions to early access programs

orphan drug development

Blogs

Mitigating risks in early access programs: A guide for biotech companies

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Thought Leadership

Get the free whitepaper: How early access programs & real-world data help Biotechs succeed

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