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Heading to World Orphan Drug Congress in Boston? Learn how we can help accelerate access to patients in Europe. Talk to our team

  • Region
    • Switzerland
Contact us
  • Region
    • Switzerland
  • Services
  • Therapeutic areas
    • Therapeutic areasOur key therapeutic areas focus on, cancer, long-term conditions and rare and orphan diseases.
    • Cancer
    • Long-term conditions
    • Rare and orphan diseases
      • Early access program services
      • Real-world data
      • Supply chain management
      • Regulatory services
      • Patient support programs
      • Market access
  • Knowledge hub
    • Knowledge hubStay up-to-date with the latest industry news, trends, insights and research. This section provides valuable information and resources.
    • Thought leaderships
    • Case studies
    • Blogs
    • Events
    • News
    • Patient stories
  • Patient hub
    • Patient hubA one-stop destination for patients to access all the essential information about our services.
    • Patient resources
    • Patient help centre
    • Life stories
    • Sciensus Intouch app
    • For new patients
      • New Patients: Where to start and what to expect
      • For cancer patients
  • Digital+
    • Digital+Digital+ is a suite of digital products and services designed to enhance patient care and improve their health outcomes.
    • Digital solutions
      • Sciensus Intouch app
      • Sciensus Cancer Companion app
      • SciensusPRO
      • Healthcare products (via Sciensus Axcess)
      • Online communities
      • Sciensus Connect
    • Patient support programs
    • Real-world data
  • About us
    • About usA leading life sciences organisation proudly sitting at the intersection of patients and their medicine.
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    • Meet our experts
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Rare diseases

Expansion into new international biotech markets can be challenging. Unfamiliar regulations and licensing, coupled with language and cultural differences, can all be barriers to growth. If you’re considering venturing into Europe and beyond, our easy-to-follow guides, shaped by 30 years of expertise in the rare disease market, will assist you in navigating challenges and gaining a profound understanding of the complexities involved in launching orphan drugs into new markets. To learn more about how Sciensus can facilitate and support your Europan expansion, visit: Rare Diseases and Orphan Drugs

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Thought Leadership, Rare diseases

Expand into Europe: unlocking the orphan drug market

Thought Leadership

Pharmacists and specialty pharmacies in rare disease commercialisation

Thought Leadership

Key strategies for a successful European drug launch

Thought Leadership

Commercialization of rare & orphan products in Switzerland and smaller EU Markets

Thought Leadership

Expand into Europe: unlocking the orphan drug market

Blogs

Rare disease day 2025

Thought Leadership

Beyond compliance: unlocking the strategic potential of PASS in rare disease therapy  

World Orphan Drug Congress USA

Events

World Orphan Drug Congress USA 2025

Blogs

The developing role of gene therapy in finding solutions to rare diseases    

EAP launch

Blogs

Strategic timing: When should biotech firms consider launching expanded access programs?   

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