We’re speaking at the Rare Trials Summit 2025
9–10 September
Sheraton Boston Hotel, Boston
Book a meetingJoin us at the Rare Trials Summit, where our experts will share forward-looking insights into the future of rare disease clinical trials. This pivotal event brings together global leaders to advance innovation, collaboration and patient-centricity in rare disease research.
Meet the Sciensus team at the Rare Trials Summit 2025
Keynote speaking sessions
The future of rare disease clinical trials: innovation, collaboration and hope
Date: 10 September
Time: 09:00-09:30
Location: Grand Liberty Ballroom
Speaker: Ray Huml
Explore how ground breaking approaches are reshaping clinical trials for rare diseases:
- Innovation in trial design – Discover how AI, decentralised trials, real-world evidence and gene therapies are transforming research and accelerating timelines
- Global collaboration – Learn how cross-border partnerships and regulatory harmonisation are essential to making rare breakthroughs a global reality
- Patient-centricity – See how involving patients early drives more inclusive, relevant and effective trial outcomes
- Equity and access – Understand the ethical imperative to ensure every patient benefits -regardless of geography or income
Walk away with a clear understanding of how a collaborative, tech-driven and patient-focused approach is transforming rare disease challenges into life-changing opportunities for patients worldwide.
The future of rare disease clinical trials
The future of rare disease clinical trials: innovation, collaboration and hope
Date: 10 September
Time: 09:00-09:30
Location: Grand Liberty Ballroom
Speaker: Ray Huml
Explore how ground breaking approaches are reshaping clinical trials for rare diseases:
- Innovation in trial design – Discover how AI, decentralised trials, real-world evidence and gene therapies are transforming research and accelerating timelines
- Global collaboration – Learn how cross-border partnerships and regulatory harmonisation are essential to making rare breakthroughs a global reality
- Patient-centricity – See how involving patients early drives more inclusive, relevant and effective trial outcomes
- Equity and access – Understand the ethical imperative to ensure every patient benefits -regardless of geography or income
Walk away with a clear understanding of how a collaborative, tech-driven and patient-focused approach is transforming rare disease challenges into life-changing opportunities for patients worldwide.
Real-world evidence that matters
Real-world evidence that matters: a hands-on workshop in building credible value stories
Date: 10 September
Time: 11:15–12:00
Location: Grand Liberty Ballroom
Speaker: Mandi Walters
Explore how to turn complex real-world data into compelling narratives that influence decisions and improve access in rare disease treatments:
- Understanding real-world evidence (RWE) – How RWE is collected, validated, and applied in rare disease contexts to complement clinical trial data
- Building credible value stories – Practical guidance on translating RWE into persuasive narratives that resonate with payers, regulators, clinicians, and patient advocates
- Collaborative approaches – Featuring perspectives from BIO and Sciensus — see how industry, patient groups, and healthcare providers align on evidence needs
- Hands-on application – Participate in interactive exercises using real-world case studies to construct and refine value stories
Leave with practical tools and strategies to transform real-world evidence into credible value stories that support stakeholder engagement and access to rare disease treatments.
We bring breakthroughs closer to rare‑disease patients
Let’s connect at Rare Trials Summit. Our tailored rare disease services simplify the journey for biopharma, healthcare professionals and – most importantly, patients. By combining scientific expertise, real-world experience and a patient-first mindset, we help accelerate progress in some of the world’s most challenging conditions.
Expertise that makes the difference
Leveraging over 30 years of clinical experience, deep therapeutic expertise and personalised digital innovation, we help biopharma, CROs and CCOs bring treatments to patients across Europe faster.
0 +
patient interactions across Europe
0
clinical deliveries annually
0 +
cancers treated via systemic anti-cancer therapies
0 +
regimens across 125 medicines
Book a meeting
Interested in meeting with our team at the event? Fill out the form below to book a time. We’ll reach out shortly to coordinate a meeting that fits your schedule. We look forward to connecting!